FDA approves Miplyffa for treatment of Niemann-Pick disease, type C
by Lori SolomonThe U.S. Food and Drug Administration has approved Zevra Therapeutics' Miplyffa (arimoclomol), an oral medication for the treatment of Niemann-Pick disease, type C (NPC).Miplyffa, i
Updated on: November 11,2024
0

FDA approves Miplyffa for treatment of Niemann-Pick disease, type C
by Lori SolomonThe U.S. Food and Drug Administration has approved Zevra Therapeutics' Miplyffa (arimoclomol), an oral medication for the treatment of Niemann-Pick disease, type C (NPC).Miplyffa, i
Updated on:November 11,2024
0
